Science & Innovation
VG712

A bivalent fusion protein: two antibody-binding domains targeting T cells attached to a truncated diphtheria toxin. VG712 binds to CD3 antigens on T cells, endocytosis delivers the toxin inside T cells and leads to cell death

Unique Molecular Structure Provides Key Differentiation
Two anti-CD3 single chain variable fragments (scFvs)
Safest T cell depletion agent to date

1Unlike monoclonal antibodies, scFVs have no Fc binding sites and therefore do not trigger lethal cytokine storm

2Truncated toxin reduces toxicity to non-CD3 cells by 1000-fold

3Half-life of 40 minutes in human body decreases risk of infection and other complications

Most efficacious T cell depletion agent to date

1Eliminates all T cell subsets since CD3 is expressed on almost all mature T cells

2Bivalency increases binding affinity to provide potent biologic activity

3Potency allows short treatment cycle: 4-day treatment is sufficient to deplete up to 99%+ of all T cells

Mechanism Of Action
Efficient cell targeting
One molecule inhibits Protein Synthesis via EF-2 disruption

Project History
1995-2007
2008-2022
2022-present
Indications and Safety Exploration

Dr. David Neville, a pioneer in immunotoxin and team invented Resimmune

Dr. Huaizhong Hu optimized molecule design for large scale production

Developed efficient and reliable production platform

Obtained global patent protection

Discovery and Development at NIH

Licensed Resimmune from NIH for development

Completed P1 clinical trial in CTCL; gained FDA Fast Track status and Orphan Drug Designation

Collaboration with U. Louisville to initiate research for anti-PD-1 combination therapy

Collaboration with U. Colorado and completed POC study for prevention of kidney transplant rejection

CMC, Clinical and Commercial Development

Virogenbio formed to license VG712 global development rights from Angimmune

CMC development completed; drug products ready for large scale clinical trials pending final FDA approval

CTCL P2 trial protocol under FDA final review

Kidney transplant P1/2 trial ready for IND submission

Formation of research and development collaboration agreement with Moffitt Cancer Center

Phase I Clinical Trial
Efficacy data from P1 trial

VG712 clears up to 99%+ of all T cell subtypes

T cell depletion is transient: after the 4-day treatment, substantially complete T cell depletion induces immediate and robust homeostatic proliferation

Proliferation peaks at up to 20 times pre-treatment levels and begins to normalize around day 90

Phase 1 Trial Efficacy

CTCL n=24, 19 patients stages 1b-2b, 5 patients stages 3-4

Overall Complete Response Rate (CRR) 17%, higher than available treatments

Response particularly robust among 14 intermediate stage patients (as measured by mSWAT lesion size score): 28% CRR, with 3 patients achieving complete remission for a duration of 6 years+ and 1 patient 4 years+

Application for P2 pivotal clinical trial currently under FDA review